| 1. |
Doudna, J. A. The promise and challenge of therapeutic genome editing. Nature. 2020, 578, 229-236.
doi: 10.1038/s41586-020-1978-5
URL
|
| 2. |
Gillmore, J. D.; Gane, E.; Taubel, J.; Kao, J.; Fontana, M.; Maitland, M. L.; Seitzer, J.; O’Connell, D.; Walsh, K. R.; Wood, K.; Phillips, J.; Xu, Y.; Amaral, A.; Boyd, A. P.; Cehelsky, J. E.; McKee, M. D.; Schiermeier, A.; Harari, O.; Murphy, A.; Kyratsous, C. A.; Zambrowicz, B.; Soltys, R.; Gutstein, D. E.; Leonard, J.; Sepp-Lorenzino, L.; Lebwohl, D. CRISPR-Cas9 in vivo gene editing for transthyretin amyloidosis. N Engl J Med. 2021, 385, 493-502.
doi: 10.1056/NEJMoa2107454
URL
|
| 3. |
van Haasteren, J.; Li, J.; Scheideler, O. J.; Murthy, N.; Schaffer, D. V. The delivery challenge: fulfilling the promise of therapeutic genome editing. Nat Biotechnol. 2020, 38, 845-855.
doi: 10.1038/s41587-020-0565-5
URL
|
| 4. |
Xu, X.; Wan, T.; Xin, H.; Li, D.; Pan, H.; Wu, J.; Ping, Y. Delivery of CRISPR/Cas9 for therapeutic genome editing. J Gene Med. 2019, 21, e3107.
|
| 5. |
Behr, M.; Zhou, J.; Xu, B.; Zhang, H. In vivo delivery of CRISPR-Cas9 therapeutics: progress and challenges. Acta Pharm Sin B. 2021, 11, 2150-2171.
doi: 10.1016/j.apsb.2021.05.020
URL
|
| 6. |
Wan, T.; Zhong, J.; Pan, Q.; Zhou, T.; Ping, Y.; Liu, X. Exosome-mediated delivery of Cas9 ribonucleoprotein complexes for tissue-specific gene therapy of liver diseases. Sci Adv. 2022, 8, eabp9435.
|
| 7. |
Kalluri, R.; LeBleu, V. S. The biology, function, and biomedical applications of exosomes. Science. 2020, 367, eaau6977.
|
| 8. |
Horodecka, K.; Düchler, M. CRISPR/Cas9: principle, applications, and delivery through extracellular vesicles. Int J Mol Sci. 2021, 22, 6072.
doi: 10.3390/ijms22116072
URL
|
| 9. |
Fang, R. H.; Kroll, A. V.; Gao, W.; Zhang, L. Cell membrane coating nanotechnology. Adv Mater. 2018, 30, e1706759.
|
| 10. |
Guo, H.; Zhang, W.; Wang, L.; Shao, Z.; Huang, X. Biomimetic cell membrane-coated glucose/oxygen-exhausting nanoreactor for remodeling tumor microenvironment in targeted hypoxic tumor therapy. Biomaterials. 2022, 290, 121821.
doi: 10.1016/j.biomaterials.2022.121821
URL
|
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